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Rare lung diseases
- Veterans Specific Activity Questionnaire (VSAQ): a new and efficient method of assessing exercise capacity in patients with pulmonary arteriovenous malformationsFilip Gawecki, Jonathan Myers, Claire L. ShovlinBMJ Open Respiratory Research Mar 2019, 6 (1) e000351; DOI: 10.1136/bmjresp-2018-000351
- Rationale, design and objectives of two phase III, randomised, placebo-controlled studies of GLPG1690, a novel autotaxin inhibitor, in idiopathic pulmonary fibrosis (ISABELA 1 and 2)Toby M Maher, Michael Kreuter, David J Lederer, Kevin K Brown, Wim Wuyts, Nadia Verbruggen, Simone Stutvoet, Ann Fieuw, Paul Ford, Walid Abi-Saab, Marlies WijsenbeekBMJ Open Respiratory Research May 2019, 6 (1) e000422; DOI: 10.1136/bmjresp-2019-000422
- Clinical use of nintedanib in patients with idiopathic pulmonary fibrosisAmy Hajari Case, Peace JohnsonBMJ Open Respiratory Research Jun 2017, 4 (1) e000192; DOI: 10.1136/bmjresp-2017-000192
- Design of the PF-ILD trial: a double-blind, randomised, placebo-controlled phase III trial of nintedanib in patients with progressive fibrosing interstitial lung diseaseKevin R Flaherty, Kevin K Brown, Athol U Wells, Emmanuelle Clerisme-Beaty, Harold R Collard, Vincent Cottin, Anand Devaraj, Yoshikazu Inoue, Florence Le Maulf, Luca Richeldi, Hendrik Schmidt, Simon Walsh, William Mezzanotte, Rozsa Schlenker-HercegBMJ Open Respiratory Research Sep 2017, 4 (1) e000212; DOI: 10.1136/bmjresp-2017-000212
- Long-term outcomes of patients with pulmonary arteriovenous malformations considered for lung transplantation, compared with similarly hypoxaemic cohortsClaire L Shovlin, Elisabetta Buscarini, J Michael B Hughes, David J Allison, James E JacksonBMJ Open Respiratory Research Oct 2017, 4 (1) e000198; DOI: 10.1136/bmjresp-2017-000198
- SARS-CoV-2 organising pneumonia: ‘Has there been a widespread failure to identify and treat this prevalent condition in COVID-19?’Pierre Kory, Jeffrey P KanneBMJ Open Respiratory Research Sep 2020, 7 (1) e000724; DOI: 10.1136/bmjresp-2020-000724
- Predictors of postoperative acute exacerbation of interstitial lung disease: a case–control studyKeisuke Hosoki, Yu Mikami, Hirokazu Urushiyama, Kunihiko Souma, Gaku Kawamura, Kanji Uchida, Takahide Nagase, Taisuke JoBMJ Open Respiratory Research Oct 2020, 7 (1) e000634; DOI: 10.1136/bmjresp-2020-000634
- Deoxynucleoside therapy for respiratory involvement in adult patients with thymidine kinase 2-deficient myopathyAna Hernandez-Voth, Javier Sayas Catalan, Marta Corral Blanco, Alba Castaño Mendez, Miguel Angel Martin, Carlos De Fuenmayor Fernandez de la Hoz, Victoria Villena Garrido, Cristina Dominguez-GonzalezBMJ Open Respiratory Research Nov 2020, 7 (1) e000774; DOI: 10.1136/bmjresp-2020-000774
- Current and future management of non-tuberculous mycobacterial pulmonary disease (NTM-PD) in the UKMarc Lipman, Joanne Cleverley, Tom Fardon, Besma Musaddaq, Daniel Peckham, Roald van der Laan, Paul Whitaker, Jacqui WhiteBMJ Open Respiratory Research Jun 2020, 7 (1) e000591; DOI: 10.1136/bmjresp-2020-000591
- The effects of sildenafil on ciliary beat frequency in patients with pulmonary non-tuberculous mycobacteria disease: phase I/II trialCedar Fowler, Un-In Wu, Robyn Shaffer, Caroline Smith, Lisa Barnhart, Clare Bryant, Kenneth Olivier, Steven M HollandBMJ Open Respiratory Research Mar 2020, 7 (1) e000574; DOI: 10.1136/bmjresp-2020-000574
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