AJRCCM: 100-Year Anniversary. Progress along the Pathway of Discovery Leading to Treatment and Cure of Cystic Fibrosis

Am J Respir Crit Care Med. 2017 May 1;195(9):1092-1099. doi: 10.1164/rccm.201702-0266ED.
No abstract available

Publication types

  • Historical Article
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Aminophenols / therapeutic use*
  • Aminopyridines / therapeutic use*
  • Anniversaries and Special Events
  • Anti-Bacterial Agents / therapeutic use*
  • Benzodioxoles / therapeutic use*
  • Chloride Channel Agonists / therapeutic use*
  • Cystic Fibrosis / drug therapy*
  • Cystic Fibrosis / genetics
  • Cystic Fibrosis / history
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Drug Combinations
  • Enzyme Replacement Therapy
  • History, 20th Century
  • History, 21st Century
  • Mutation
  • Periodicals as Topic / history*
  • Pulmonary Medicine / history*
  • Quinolones / therapeutic use*

Substances

  • Aminophenols
  • Aminopyridines
  • Anti-Bacterial Agents
  • Benzodioxoles
  • CFTR protein, human
  • Chloride Channel Agonists
  • Drug Combinations
  • Quinolones
  • lumacaftor, ivacaftor drug combination
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • ivacaftor