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Rare lung diseases
- Prospectively evaluating maternal and fetal outcomes in the era of CFTR modulators: the MAYFLOWERS observational clinical trial study designRaksha Jain, Amalia Magaret, Phuong T Vu, Jill M VanDalfsen, Ashley Keller, Alexandra Wilson, Melissa S Putman, Nicole Mayer-Hamblett, Charles R Esther, Jennifer L Taylor-CousarBMJ Open Respiratory Research Jun 2022, 9 (1) e001289; DOI: 10.1136/bmjresp-2022-001289
- Genomic testing for children with interstitial and diffuse lung disease (chILD): parent satisfaction, understanding and health-related quality of lifeLauren Kelada, Claire Wakefield, Nada Vidic, David S Armstrong, Bruce Bennetts, Kirsten Boggs, John Christodoulou, Joanne Harrison, Gladys Ho, Nitin Kapur, Suzanna Lindsey-Temple, Tim McDonald, David Mowat, André Schultz, Hiran Selvadurai, Andrew Tai, Adam JaffeBMJ Open Respiratory Research Feb 2022, 9 (1) e001139; DOI: 10.1136/bmjresp-2021-001139
- Novel method to select meaningful outcomes for evaluation in clinical trialsCharlie McLeod, Richard Norman, Jamie Wood, Siobhain Mulrennan, Sue Morey, André Schultz, Mitch Messer, Kate Spaapen, Matthew Stoneham, Yue Wu, Alan Smyth, Christopher Blyth, Steve Webb, Steven Mascaro, Owen Woodberry, Tom SnellingBMJ Open Respiratory Research Oct 2021, 8 (1) e000877; DOI: 10.1136/bmjresp-2021-000877
- Cardiopulmonary function in adolescent patients with pectus excavatum or carinatumSalim Ramadan, Jim Wilde, Anne Tabard-Fougère, Seema Toso, Maurice Beghetti, Jean-Paul Vallée, Regula Corbelli, Constance Barazzone-Argiroffo, Pierre Lascombes, Isabelle Ruchonnet-MétraillerBMJ Open Respiratory Research Jul 2021, 8 (1) e001020; DOI: 10.1136/bmjresp-2021-001020
- Utility of radial endobronchial ultrasonography combined with transbronchial lung cryobiopsy in patients with diffuse parenchymal lung diseases: a multicentre prospective studyMinoru Inomata, Naoyuki Kuse, Nobuyasu Awano, Mari Tone, Hanako Yoshimura, Tatsunori Jo, Jonsu Minami, Kohei Takada, Yutaka Muto, Kazushi Fujimoto, Akinori Harada, Yuan Bae, Toshio Kumasaka, Hideaki Yamakawa, Shintaro Sato, Kazunori Tobino, Hidekazu Matsushima, Tamiko Takemura, Takehiro IzumoBMJ Open Respiratory Research Jan 2021, 8 (1) e000826; DOI: 10.1136/bmjresp-2020-000826
- Deoxynucleoside therapy for respiratory involvement in adult patients with thymidine kinase 2-deficient myopathyAna Hernandez-Voth, Javier Sayas Catalan, Marta Corral Blanco, Alba Castaño Mendez, Miguel Angel Martin, Carlos De Fuenmayor Fernandez de la Hoz, Victoria Villena Garrido, Cristina Dominguez-GonzalezBMJ Open Respiratory Research Nov 2020, 7 (1) e000774; DOI: 10.1136/bmjresp-2020-000774
- Predictors of postoperative acute exacerbation of interstitial lung disease: a case–control studyKeisuke Hosoki, Yu Mikami, Hirokazu Urushiyama, Kunihiko Souma, Gaku Kawamura, Kanji Uchida, Takahide Nagase, Taisuke JoBMJ Open Respiratory Research Oct 2020, 7 (1) e000634; DOI: 10.1136/bmjresp-2020-000634
- SARS-CoV-2 organising pneumonia: ‘Has there been a widespread failure to identify and treat this prevalent condition in COVID-19?’Pierre Kory, Jeffrey P KanneBMJ Open Respiratory Research Sep 2020, 7 (1) e000724; DOI: 10.1136/bmjresp-2020-000724
- Current and future management of non-tuberculous mycobacterial pulmonary disease (NTM-PD) in the UKMarc Lipman, Joanne Cleverley, Tom Fardon, Besma Musaddaq, Daniel Peckham, Roald van der Laan, Paul Whitaker, Jacqui WhiteBMJ Open Respiratory Research Jun 2020, 7 (1) e000591; DOI: 10.1136/bmjresp-2020-000591
- The effects of sildenafil on ciliary beat frequency in patients with pulmonary non-tuberculous mycobacteria disease: phase I/II trialCedar Fowler, Un-In Wu, Robyn Shaffer, Caroline Smith, Lisa Barnhart, Clare Bryant, Kenneth Olivier, Steven M HollandBMJ Open Respiratory Research Mar 2020, 7 (1) e000574; DOI: 10.1136/bmjresp-2020-000574
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